EVERYDAY SCIENCE

Detailed explanation-1: -If the treatment is successful, the new gene delivered by the vector will make a functioning protein or the editing molecules will correct a DNA error and restore protein function. Gene therapy with viral vectors has been successful, but it does carry some risk. Sometimes the virus triggers a dangerous immune response.

Detailed explanation-2: -Several inherited immune deficiencies have been treated successfully with gene therapy. Most commonly, blood stem cells are removed from patients, and retroviruses are used to deliver working copies of the defective genes. After the genes have been delivered, the stem cells are returned to the patient.

Detailed explanation-3: -Gene therapy can actually be considered a form of protein therapy.

Detailed explanation-4: -So different cell types “turn on” different genes, allowing different proteins to be made. This gives different cell types different functions. Once a gene is expressed, the protein product of that gene is usually made. For this reason, gene expression and protein synthesis are often considered the same process.

Detailed explanation-5: -Gene expression is the process by which the information encoded in a gene is turned into a function. This mostly occurs via the transcription of RNA molecules that code for proteins or non-coding RNA molecules that serve other functions.