PATHOLOGY

Detailed explanation-1: -Clinical trials of gene therapy in people have shown some success in treating certain diseases, such as: Severe combined immune deficiency. Hemophilia. Blindness caused by retinitis pigmentosa.

Detailed explanation-2: -A large proportion of the candidates for gene therapy include advanced-stage cancer or hematological conditions. In addition, rare or inherited disorders are also frequent targets of gene therapy.

Detailed explanation-3: -There are basically three types of gene therapy: ex vivo, in vivo, and in situ.

Detailed explanation-4: -Genetic conditions or disorders that arise from mutations in a single gene are ideal candidates for gene therapy.

Detailed explanation-5: -Immune deficiencies. Several inherited immune deficiencies have been treated successfully with gene therapy. Hereditary blindness. Hemophilia. Blood disease. Fat metabolism disorder. Cancer.